Klaus Veitinger

Cure Rare Disease is a nonprofit biotechnology company whose mission is to enable and finance the development of life-saving genetic medicines for rare and ultra-rare patient populations previously deemed too rare to treat. To realize this, our unique ecosystem facilitates collaboration between world-renowned researchers and clinicians, policy experts and our generous donors. Together, we are fundamentally changing the rare and ultra-rare disease experience and burden for millions of people around the world with our discoveries and methods—while bringing hope to patients waiting for a cure.

scPharmaceuticals is a clinical-stage pharmaceutical company focused on developing and commercializing products that, through our proprietary platform, are designed to enable the subcutaneous administration of therapies previously limited to intravenous (IV) delivery—with the goal of transforming infused therapies, advancing patient care, and reducing healthcare costs.

We are a biopharmaceutical company and wholly owned subsidiary of Alfasigma S.p.A. focused on the development and commercialization of novel therapeutics to treat rare and serious liver diseases, including primary biliary cholangitis (PBC) and severe alcohol-associated hepatitis (sAH). In a new age of liver disease treatment, our team is developing vital therapies to meet the needs of those living with rare and serious liver disease. We are committed to improving patients’ lives and addressing the liver community’s most pressing needs. Our corporate headquarters is located in New Jersey. For more information about Intercept, please visit our website at: www.interceptpharma.com and follow us on X at: @InterceptPharma.

Synageva BioPharma is a biopharmaceutical company dedicated to discovering, developing, and delivering innovative medicines for people living with rare diseases of high unmet medical need. We are passionate about our commitment to improving their lives and those of their families for generations to come. Our experienced team has helped bring several life-saving therapies for diseases that were once considered too rare for development treatments. We believe that every patient deserves treatment options, no matter how rare their disease. We believe that when it comes to delivering innovative therapies, Every Second Counts.

Cure Rare Disease is a nonprofit biotechnology company whose mission is to enable and finance the development of life-saving genetic medicines for rare and ultra-rare patient populations previously deemed too rare to treat. To realize this, our unique ecosystem facilitates collaboration between world-renowned researchers and clinicians, policy experts and our generous donors. Together, we are fundamentally changing the rare and ultra-rare disease experience and burden for millions of people around the world with our discoveries and methods—while bringing hope to patients waiting for a cure.

Every year in the U.S., nearly 2 million are diagnosed with cancer. Traditional cancer surgery, chemotherapy and radiation give patients precious moments but no long-term promise. New cancer therapies using the body’s own cells and genes are changing this. In 2001, Alliance for Cancer Gene Therapy became one of the first and only organizations to embrace a progressive vision for the underfunded but exceptionally promising discipline of cancer cell and gene therapy. The organization quickly became a catalytic force in shaping entirely new cancer treatment models by identifying, funding, and advancing the most innovative and impactful translational research in cell and gene therapies. To date, we have awarded more than $30 million in grants to world class cancer researchers representing the top medical institutions in the U.S. and Canada, advancing new approaches to leukemia, lymphoma, ovarian, prostate, sarcoma, glioblastoma, melanoma, lung and pancreatic cancers. It’s time for another breakthrough: Today there is an urgent need to translate the profound success of CAR T-cell therapies for blood cancers into successful therapies for the most complex and deadly cancers – solid tumor cancers. Current funding priorities work to tackle pancreatic cancer and brain cancer, and to advance the understanding of solid tumor biology that will lead to curative therapies. Help advance our vision for a cure to all cancers. 100% of public donations directly support frontline scientists and programs working on thoroughly vetted and responsibly monitored cancer cell and gene therapy research enabling Alliance for Cancer Gene Therapy to award $34.2 million through 67 grants to 63 innovative researchers, representing 38 top medical institutions in the U.S. and Canada.

scPharmaceuticals is a clinical-stage pharmaceutical company focused on developing and commercializing products that, through our proprietary platform, are designed to enable the subcutaneous administration of therapies previously limited to intravenous (IV) delivery—with the goal of transforming infused therapies, advancing patient care, and reducing healthcare costs.

We are a biopharmaceutical company and wholly owned subsidiary of Alfasigma S.p.A. focused on the development and commercialization of novel therapeutics to treat rare and serious liver diseases, including primary biliary cholangitis (PBC) and severe alcohol-associated hepatitis (sAH). In a new age of liver disease treatment, our team is developing vital therapies to meet the needs of those living with rare and serious liver disease. We are committed to improving patients’ lives and addressing the liver community’s most pressing needs. Our corporate headquarters is located in New Jersey. For more information about Intercept, please visit our website at: www.interceptpharma.com and follow us on X at: @InterceptPharma.

OrbiMed invests globally across the healthcare industry, from start-ups to large multinational corporations, through a range of private equity funds, public equity funds, and royalty/credit funds. OrbiMed seeks to be a capital provider of choice, providing tailored financing solutions and extensive global team resources to help build world-class healthcare companies. OrbiMed’s team of over 100 professionals is based in New York City, San Francisco, Shanghai, Hong Kong, Mumbai, Herzliya, and other key global markets.